Emirati girl with spinal muscular atrophy takes her first few steps at Abu Dhabi long-term care hospital – Gulf News Tuesday, 22 February, 2022 Gulf News
UK Expands Referral Criteria for Zolgensma to Heavier Children – SMA News Today Wednesday, 2 February, 2022 SMA News Today
Baby given months to live may now outlive parents – after receiving world’s most expensive drug – National World Monday, 10 January, 2022 NationalWorld
As trials lag on Risdiplam’s effectiveness in adults, the drug remains out of reach for many – ABC News Thursday, 9 December, 2021 abc News