UK Expands Referral Criteria for Zolgensma to Heavier Children – SMA News Today Wednesday, 2 February, 2022 SMA News Today
Baby given months to live may now outlive parents – after receiving world’s most expensive drug – National World Monday, 10 January, 2022 NationalWorld
As trials lag on Risdiplam’s effectiveness in adults, the drug remains out of reach for many – ABC News Thursday, 9 December, 2021 abc News
Gene Therapy Improves Muscle Function for Children With Spinal Muscular Atrophy – Technology Networks Tuesday, 30 November, 2021 Technology Networks