The family desperate for a miracle drug that could help their son walk and talk – Manchester Evening News Monday, 15 February, 2021 Manchester Evening News
Eight-week-old baby with spinal muscular atrophy could be saved by a single jab – Daily Mail Tuesday, 15 December, 2020 Daily Mail
Canadian baby with spinal muscular atrophy to get ‘world’s most expensive drug’ – CTV News Tuesday, 20 October, 2020 CTV News
From no drugs to 3: Patients with spinal muscular atrophy now face hard choices – BioPharma Dive Monday, 5 October, 2020 BioPharma Dive
How advances are changing the standard of care for patients with spinal muscular atrophy – Pharmafield Thursday, 27 August, 2020 Pf Media
Coronavirus: The shielders turning the word ‘vulnerable’ on its head – BBC News Friday, 31 July, 2020 BBC News
Girl struggling to walk denied NHS drug because she took one step too few – Liverpool Echo Thursday, 18 June, 2020 Liverpool Echo
Engineers supporting children’s learning during COVID-19 lockdown – The Engineer Wednesday, 29 April, 2020 The Engineer
Should Biogen’s Spinraza for SMA be delayed amid COVID-19? No, say these parents – FiercePharma Thursday, 26 March, 2020 Fierce Pharma
Positive disability stories you might have missed in March 2020 – Disability Horizons Saturday, 21 March, 2020 Disability Horizons
Toddler with fatal illness ‘recovers’ after $2m infusion of world’s dearest drug – Metro.co.uk Tuesday, 25 February, 2020 Metro News
Ill boy, 2, dies after ‘cruel dad blows £115,000 crowdfunding donations on brothels, luxury holidays and drugs – The Sun Thursday, 24 October, 2019 The Sun
Newcomer BillionToOne launches prenatal blood screener for cystic fibrosis, SMA and sickle cell – FierceBiotech Monday, 1 July, 2019 Fierce Biotech
New gene therapy poised to transform care for spinal muscular atrophy – Medical Xpress Saturday, 8 June, 2019 medicalxpress.com
Six-month-old boy has just months to live after the NHS refuse to pay for a ‘miracle drug’ – Daily Mail Wednesday, 27 February, 2019 Daily Mail
Scientists investigate new strategy to treat spinal muscular atrophy in infants – Medical Xpress Thursday, 7 June, 2018 medicalxpress.com
Spinal muscular atrophy (SMA) patients could get access to drug earlier than expected – Daily Mail Friday, 19 January, 2018 Daily Mail
‘We don’t know how long we’ve got her for’: First-time parents share anguish as they spend their final moments with their terminally ill baby daughter born with a rare muscle-wasting disease – Daily Mail Monday, 7 August, 2017 Daily Mail
Communicative development inventory in type 1 and presymptomatic infants with spinal muscular atrophy: a cohort study Thursday, 18 April, 2024 BMJ Journal
New test to identify Spinal Muscular Atrophy in babies launches in Wessex Friday, 10 November, 2023 ITV News
14-Year-Old Girl with Rare Genetic Disorder Gets to Attend Her First-Ever Concert, Taylor Swift’s ‘Eras Tour’ Thursday, 27 April, 2023 Yahoo News
