Paediatric patient with spinal muscular atrophy to get first gene therapy in BD – The Financial Express Monday, 24 October, 2022 The financial express
Should Treatment for Spinal Muscular Atrophy Be Initiated Earlier? – Neurology Advisor Friday, 14 October, 2022 Neurology Advisor
Roy Hodgson leads Down’s Syndrome Eagles training – Palace For Life Foundation Friday, 14 October, 2022 Neurology Advisor
At a fashion show for people with spinal muscular atrophy, models take back their own stories – STAT Friday, 16 September, 2022 Stat News
Listing breakthrough brings hope for people with spinal condition – The Sydney Morning Herald Monday, 1 August, 2022 The Sidney Morning Herald
University of Oxford: First UK pilot study of newborn screening for spinal muscular atrophy launched in Oxford – India Education Diary Monday, 14 March, 2022 India Education Diary
First UK pilot study of newborn screening for spinal muscular atrophy launched in Oxford – University of Oxford Friday, 11 March, 2022 University of Oxford
Emirati girl with spinal muscular atrophy takes her first few steps at Abu Dhabi long-term care hospital – Gulf News Tuesday, 22 February, 2022 Gulf News
UK Expands Referral Criteria for Zolgensma to Heavier Children – SMA News Today Wednesday, 2 February, 2022 SMA News Today
Baby given months to live may now outlive parents – after receiving world’s most expensive drug – National World Monday, 10 January, 2022 NationalWorld
As trials lag on Risdiplam’s effectiveness in adults, the drug remains out of reach for many – ABC News Thursday, 9 December, 2021 abc News
Gene Therapy Improves Muscle Function for Children With Spinal Muscular Atrophy – Technology Networks Tuesday, 30 November, 2021 Technology Networks
NICE recommends risdiplam for spinal muscular atrophy – European Pharmaceutical Review Wednesday, 24 November, 2021 European pharmaceutical review
Tokyo 2020 Paralympics led to better understanding of people with disabilities – Inside the games Monday, 8 November, 2021 Inside The Games
Ideal Therapy Aids Motor Skills and Breathing, Taken Orally: UK Survey – SMA News Today Monday, 1 November, 2021 SMA News Today
Significant boost for children with Spinal Muscular Atrophy as new gene therapy is approved for use in Ireland – Irish Medical Times Friday, 8 October, 2021 Irish Medical Times
Babies with SMA able to swallow with Evrysdi® treatment – European Pharmaceutical Review Friday, 24 September, 2021 European pharmaceutical review
‘It really is a miracle drug’: Yorkshire boy with spinal muscular atrophy receives ‘most expensive drug in the world’ at Sheffield Children’s Hospital – The Yorkshire Post Thursday, 16 September, 2021 Yorkshire Post
Spinal Muscular Atrophy: Why An Early Diagnosis And Treatment Is Crucial For Patients – ABP Live Monday, 13 September, 2021 ABP Live
Risdiplam improves motor function in infants with spinal muscular atrophy – Medical Xpress Friday, 20 August, 2021 Medical Xpress
Scholar Rock Announces Apitegromab Meets Primary Endpoint in Phase 3 SAPPHIRE Study in Patients with Spinal Muscular Atrophy (SMA) Monday, 7 October, 2024 Cure SMA
Mom says at-home treatment for Spinal Muscular Atrophy boosted daughter’s care Monday, 26 August, 2024 MSN
