Spinal muscular atrophy: Spinraza approval delights family – BBC News

The mother of a girl with a muscle-wasting disease is delighted a drug that may slow her daughter’s condition has been approved for use on the NHS.

NHS England said it has agreed the use of Spinraza to treat spinal muscular atrophy (SMA).

Heidi Prescott-Booth, 11, from Wolverhampton, was diagnosed with the condition when she was three.

Her mother, Katie Prescott, said they are “over the moon” that she will be able to access the drug.

SMA is a genetic condition which affects the nerves in the spinal cord, weakening muscles and causing problems with movement, breathing and swallowing.

It can significantly reduce life expectancy when it develops in babies and toddlers.

For Heidi, the condition means she struggles to walk.

Mrs Prescott said: “We are speechless, it is incredible. When Heidi found out she just cried her eyes out.”

Read more at: https://www.bbc.com/news/uk-england-birmingham-48275002

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