How advances are changing the standard of care for patients with spinal muscular atrophy – Pharmafield

This August is Spinal Muscular Atrophy (SMA) Awareness Month. It’s the perfect time to celebrate recent advances in treatment of this rare condition, which are inspiring hope for the 660–1320 children and adults living with SMA in the UK (1).

What is SMA?

Spinal muscular atrophy is a rare inherited muscle-wasting disease that is complex, debilitating and life-threatening. Symptoms include progressive muscle loss that consequently affects arm, hand, head and neck movement. This limits a person’s ability to walk, eat and ultimately, breathe (2,3).

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