Neural Stem Cell Transplants May Delay Progression of SMARD1 – SMA News Today
Transplanting a subset of neural stem cells (NSCs) to…
Area toddler faces challenges with Spinal Muscular Atrophy Type 1 – Vinton Today
LyRick, a little Vinton resident, is in a fight for his life…
‘Children’s services need to integrate to improve – here’s how’ – Communitycare.co.uk
It is indisputable that children’s…
Across SMA Types, Swallowing and Speech Problems Can Be Common, Study Finds – SMA News Today
Swallowing and speech problems are common in both children…
Russia Approves Spinraza to Treat All SMA Patients – SMA News Today
Olga and Andrew Fuks with their children, Katya and Oscar, both of…
The devastating reason Scott Morrison has stood behind children battling spinal muscular atrophy – Daily Mail
Jenny Morrison met Roslyn Krouskos through her daughters’ school…
Health insurance companies deny kids with SMA gene therapy Zolgensma – Business Insider
The health insurer Anthem Blue Cross Blue Shield has denied Jackson Schultheis…
’31 Days of SMA’ Among Highlights of August, SMA Awareness Month – SMA News Today
SMA News Today, having launched forums and added regular columnists, is now running a month-long series to…
31 Days of SMA: Confronting an SMA Diagnosis – SMA News Today
Day 4 of 31 Days of SMA⠀ Topic: Confronting and SMA Diagnosis⠀ This is Byron’s Story:⠀ ⠀ It’s March 19th, 2015…
31 Days of SMA: Employment and SMA – SMA News Today
31 Days of SMA⠀ To start off SMA Awareness Month, we have Jaclyn Greenwood speaking on employment and…
Wheelchair bound Bristol teen fighting ‘immensely cruel’ decision to bar him from life changing drug – Bristol Post
A Bristol teenager is in a fight against “discriminatory” and “immensely cruel” health guidelines that are barring…
Hayes in the House: MP talks about his casework and focuses on spinal muscular atrophy – Spalding Today
In this spirit, when Tanya White contacted me about her daughter Rae’s medical needs, I learned a…
Enhancing the Quality of Life for Patients with Spinal Muscular Atrophy – ThirdAge
Spinal Muscular Atrophy (SMA) is the umbrella term for a group of genetic disorders that cause muscle…
Meet Jake – a 13-year-old theatre trailblazer – CBBC Newsround
Meet Jake. He loves the magic of theatre – the props, the costumes and bringing characters to…
Biogen spinal muscular atrophy drug shows strong data in long-term follow-up – MedCity News
Updated Phase II data on a drug used to treat spinal muscular atrophy show strong efficacy among…
Newcomer BillionToOne launches prenatal blood screener for cystic fibrosis, SMA and sickle cell – FierceBiotech
The company’s molecule-counting diagnostic test, Unity, searches for cell-free fetal DNA using…
Campaign girl ‘ineligible’ for muscle wasting drug – BBC News
The family of a girl who campaigned for a drug to treat her muscle-wasting disease to be…
New gene therapy poised to transform care for spinal muscular atrophy – Medical Xpress
The University of Rochester Medical Center (URMC) has been tapped as one of the first institutions in…
Spinal muscular atrophy: Spinraza approval delights family – BBC News
The mother of a girl with a muscle-wasting disease is delighted a drug that may slow her…
Wolverhampton mum calls for decision on use of Spinraza – BBC News
The mother of an 11-year-old girl with a muscle-wasting disease is calling for health chiefs to speed…