31 Days of SMA: Employment and SMA – SMA News Today
31 Days of SMA⠀ To start off SMA Awareness Month, we have Jaclyn Greenwood speaking on employment and…
Wheelchair bound Bristol teen fighting ‘immensely cruel’ decision to bar him from life changing drug – Bristol Post
A Bristol teenager is in a fight against “discriminatory” and “immensely cruel” health guidelines that are barring…
Hayes in the House: MP talks about his casework and focuses on spinal muscular atrophy – Spalding Today
In this spirit, when Tanya White contacted me about her daughter Rae’s medical needs, I learned a…
Enhancing the Quality of Life for Patients with Spinal Muscular Atrophy – ThirdAge
Spinal Muscular Atrophy (SMA) is the umbrella term for a group of genetic disorders that cause muscle…
Meet Jake – a 13-year-old theatre trailblazer – CBBC Newsround
Meet Jake. He loves the magic of theatre – the props, the costumes and bringing characters to…
Biogen spinal muscular atrophy drug shows strong data in long-term follow-up – MedCity News
Updated Phase II data on a drug used to treat spinal muscular atrophy show strong efficacy among…
Newcomer BillionToOne launches prenatal blood screener for cystic fibrosis, SMA and sickle cell – FierceBiotech
The company’s molecule-counting diagnostic test, Unity, searches for cell-free fetal DNA using…
Campaign girl ‘ineligible’ for muscle wasting drug – BBC News
The family of a girl who campaigned for a drug to treat her muscle-wasting disease to be…
New gene therapy poised to transform care for spinal muscular atrophy – Medical Xpress
The University of Rochester Medical Center (URMC) has been tapped as one of the first institutions in…
Spinal muscular atrophy: Spinraza approval delights family – BBC News
The mother of a girl with a muscle-wasting disease is delighted a drug that may slow her…
Wolverhampton mum calls for decision on use of Spinraza – BBC News
The mother of an 11-year-old girl with a muscle-wasting disease is calling for health chiefs to speed…
Adapting to Change Creatively – SMA News Today
Spinal muscular atrophy (SMA) can cause a lot of things, including muscle weakness, fatigue, and pain. It’s…
Finding a Perfect Parking Spot: It’s Complicated – SMA News Today
We’ve all had some cruddy parking experiences. But when you have a disability, it’s usually a little…
The Power of a Platform – SMA News Today
I’ve been meaning to update my website for years, so I sat down in January with the…
New Hope for Young Children with SMA – Early Treatment is Key – MD Magazine
No parent wants to hear their pediatrician give this diagnosis, “Your child has spinal muscular atrophy (SMA).”…
My daughter is losing the ability to walk but she is being denied drugs that can help – Metro
As a parent you never want your child to be ill. And when they are, you want…
Six-month-old boy has just months to live after the NHS refuse to pay for a ‘miracle drug’ – Daily Mail
A six-month-old boy with a devastating genetic condition has been given just three months to live unless…
This gorgeous baby boy has only three months to live unless the NHS decides to fund a miracle drug – Manchester Evening News
Lying in the Intensive Care Unit of Royal Manchester Children’s Hospital, baby Haris Khan listens to some…
British MP Pushes to Make Spinraza Treatment Available for SMA Patients – SMA News Today
Citing the deteriorating health of a child with spinal muscular atrophy (SMA), a member of the British…
Scotland Opens Spinraza to All SMA Patients Using Its Public Health System – SMA News Today
Scotland has joined the growing roster of countries making the spinal muscular atrophy (SMA) therapy Spinraza available…