Spinal muscular atrophy

Girl struggling to walk denied NHS drug because she took one step too few – Liverpool Echo

  A…

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Study: Heart Problems in SMA May Be Tied to Calcium Dysregulation – SMA News Today

Heart problems associated with spinal muscular atrophy (SMA) may be caused partially by calcium dysregulation…

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SMA Patients in England Can Now Access 3 More Spinraza Treatment Sites – SMA News Today

With the addition of these centers, there are now 11 National Health Service Foundation Trust…

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Too Little Known About Care Needs of Adults with SMA, Study Says – SMA News Today

A better understanding of the needs of adults with spinal muscular atrophy (SMA), best ensuring…

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Managing SMA Is Like an Ongoing Chess Match – SMA News Today

  Puzzles are all the rage these…

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Time Is Motor Neurons A father’s perspective: Our journey to finding a treatment – SMA News Today

When Quinn, our soon-to-be-born daughter, didn’t make as much movement in the womb as our…

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Evidence Points to Benefits of Newborn Screening for SMA, German Researchers Say – SMA News Today

Researchers in Germany have found that newborn screening for spinal muscular atrophy (SMA) would likely…

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Interplay of Motor Neurons and Glial Cells at Root of SMA, Review Suggests – SMA News Today

The interplay between different types of nerve cells, including motor neurons and glial cells, seems…

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Engineers supporting children’s learning during COVID-19 lockdown – The Engineer

With many schools closed, Primary Engineer’s ‘If you were an engineer, what would you do?’ competition is now available for school pupils to…

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Growth-friendly Spinal Implants May Help SMA Children Before Fusion Surgery – SMA News Today

Spinal fusion surgery — a procedure to fuse two or more spine vertebrae — is…

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This Influencer Has Spinal Muscular Atrophy Type 2 and It Inspired Her to Make a Size-Inclusive Clothing Line – Health.com

  Our series This Is Me is about being empowered to…

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Should Biogen’s Spinraza for SMA be delayed amid COVID-19? No, say these parents – FiercePharma

Biogen said it is working with families and healthcare providers to try…

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Information About COVID-19 for SMA Patients – SMA News Today

  COVID-19, short for coronavirus disease 2019, is…

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Composite materials help bring revolutionary exoskeleton to life – British Plastics and Rubber

The University of Central Lancashire’s Engineering Innovation Centre has…

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Toddler with fatal illness ‘recovers’ after $2m infusion of world’s dearest drug – Metro.co.uk

Two year-old Maddy Smith has made a miraculous recovery from a crippling…

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Treatment with Risdiplam Improves Motor Function in Spinal Muscular Atrophy – Drug Topics

Risdiplam, an investigational drug for the treatment of spinal…

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When a lottery ‘wins’ sick babies life-saving drugs – BBC News

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Roche’s risdiplam achieves endpoint in spinal muscular atrophy trial – Pharmaceutical Business Review

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Roche Starts Early Access Program for SMA Therapy Risdiplam in Europe – SMA News Today

Roche has kicked off a worldwide early access program…

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Top 10 SMA Stories of 2019 – SMA News Today

SMA News Today brought you daily coverage of key…

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