Top 5 Most-Read SMA Stories of 2020 – AJMC.com Managed Markets Network
The top 5 most-read stories about spinal muscular atrophy (SMA) of 2020 on AJMC.com focused…
Eight-week-old baby with spinal muscular atrophy could be saved by a single jab – Daily Mail
Like a ‘punch in the stomach’, is how Megan Willis felt on hearing that her…
From no drugs to 3: Patients with spinal muscular atrophy now face hard choices – BioPharma Dive
Jud Broadhurst was 14 years old when he…
Study Findings Offer More Understanding of Natural History of Type III SMA – AJMC
By assessing longitudinal changes in functional status, researchers are offering a better understanding of the…
How advances are changing the standard of care for patients with spinal muscular atrophy – Pharmafield
This August is Spinal Muscular Atrophy (SMA) Awareness Month. It’s the perfect time to celebrate…
Treatment Is Key for All With SMA, But Gains Will Differ – SMA News Today
Treating newborns whose spinal muscular atrophy (SMA) is discovered in screening programs — before symptoms…
How different generations living with SMA can teach one another – SMA News Today
Paying it forward Meet Regina and Al. Their friendship and respect for one another all started…
Coronavirus: The shielders turning the word ‘vulnerable’ on its head – BBC News
This weekend shielding will officially stop. The ‘elderly and vulnerable’ who have followed stringent rules will re-join society and follow the same social…
Wheelchair-bound man slams insurance company over rejected claim – Daily Mail
A wheelchair-bound man who is almost completely paralyzed has called out his private insurance company…
Phase 4 Nusinersen Trial Underway in Infants, Children With Spinal Muscular Atrophy – Pharmacy Times
A phase 4 study is underway to assess the safety of nusinersen (Spinraza, Biogen) in…
Disparities Found in Parents, Children’s Perceptions of SMA – SMA News Today
Perceptions about illness often don’t line up between children with spinal muscular atrophy (SMA) and…
Study: Heart Problems in SMA May Be Tied to Calcium Dysregulation – SMA News Today
Heart problems associated with spinal muscular atrophy (SMA) may be caused partially by calcium dysregulation…
SMA Patients in England Can Now Access 3 More Spinraza Treatment Sites – SMA News Today
With the addition of these centers, there are now 11 National Health Service Foundation Trust…
Too Little Known About Care Needs of Adults with SMA, Study Says – SMA News Today
A better understanding of the needs of adults with spinal muscular atrophy (SMA), best ensuring…
Managing SMA Is Like an Ongoing Chess Match – SMA News Today
Puzzles are all the rage these…
Time Is Motor Neurons A father’s perspective: Our journey to finding a treatment – SMA News Today
When Quinn, our soon-to-be-born daughter, didn’t make as much movement in the womb as our…
Evidence Points to Benefits of Newborn Screening for SMA, German Researchers Say – SMA News Today
Researchers in Germany have found that newborn screening for spinal muscular atrophy (SMA) would likely…