Muscular Dystrophy

LAMA2 Muscular Dystrophy Drug Candidate TXA127 Is Granted Orphan Drug Status – Muscular Dystrophy News

Tarix Orphan LLC recently announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug designation to TXA127, the company’s lead…

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Muscle Proteins May Serve as Serum Biomarkers for 3 Types of Muscular Dystrophy – Muscular Dystrophy News

Pfizer, in collaboration with Newcastle University, reports finding four serum biomarkers for three types of muscular dystrophy. The markers may be valuable for…

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CSU alum named National Goodwill Ambassador by Muscular Dystrophy Association – Rocky Mountain Collegian

The Muscular Dystrophy Association recently named 2013 Colorado State University alum Joseph Akmakjian its National Goodwill Ambassador. This is the first year the…

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New approach could be used to treat Duchenne muscular dystrophy – News-Medical.net

Scientists at the UCLA Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research and Center for Duchenne Muscular Dystrophy at…

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Jimboy’s Tacos Raises $11000 for Muscular Dystrophy – QSR magazine (press release) (registration)

Jimboy’s Tacos, the fast-casual, American-style Mexican food chain announced it raised more than $11,000 for the Muscular Dystrophy Association (MDA) during its annual…

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Muscular Dystrophy Drugs Face New FDA Questions – Wall Street Journal

Hopes are dimming that the drug industry will be able to quickly deliver a treatment for one of the most keenly researched diseases…

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Pupils ‘Go Orange’ to raise money for muscular dystrophy charity – Gravesend Reporter

Pupils at Shears Green Junior School in Gravesend donned orange clothes on Friday as part of a fundraiser for a muscular disorder charity….

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Stem cell gene therapy could be key to treating Duchenne muscular dystrophy – UC Los Angeles

Scientists at the UCLA Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research and Center for Duchenne Muscular Dystrophy at…

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Man with muscular dystrophy to walk three miles for friend – St Helens Star

AFTER a friend raised money for him last year, a man with muscular dystrophy is taking on a three-mile walk to return the…

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Boy With Muscular Dystrophy Writes Heartfelt Note to Scottish Leader – The Mighty

Michael Young, 9, wrote a letter to Scottish first minister Nicola Sturgeon, urging her to help make the drug Translarna available for people…

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Duchenne muscular dystrophy: direct effect on muscle stem cells? An interview with Dr Rudnicki – News-Medical.net

News-Medical.net This understanding is still correct and this is the driver of the muscle damage in Duchenne muscular dystrophy. Our discovery is really a…

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CSU alum named new spokesperson for Muscular Dystrophy Association – Colorado State University News (press release)

Colorado State University News (press release) A Colorado State University alumnus has been named the first adult National Goodwill Ambassador for the Muscular Dystrophy…

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Twins Zia and Cyanne Westerman BOTH born with Muscular Dystrophy – Daily Mail

The 24-year-old twins were born with Muscular Dystrophy – a debilitating condition that will be with them for life. ‘It’s a weakness of…

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Southport school hosts ‘Go Orange Day’ to raise awareness of muscular dystrophy – Southport Visiter

To raise awareness, a Muscular Dystrophy UK spokesperson, Mr Houghton, was invited along to give more information about the condition to the pupils,…

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Young boy with muscular dystrophy lobbies Nicola Sturgeon – BBC News

A nine-year-old boy with muscular dystrophy has met with First Minister Nicola Sturgeon after he wrote to her campaigning for a new treatment….

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Nine-year-old boy in appeal to Nicola Sturgeon over muscular dystrophy treatment – Herald Scotland

Michael Young, from Larbert near Falkirk, is thought to be one of five children in Scotland that could benefit from Translarna, the first…

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Gene editing shows promise in treating muscular dystrophy – Ars Technica UK

Several new experiments published in Science demonstrate that we can now edit the genomes of mice with muscular dystrophy, effectively restoring a large…

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