NHS to offer ‘world’s most expensive’ £1.8m-a-dose drug to cure baby spinal disease – Daily Mail March 19, 2023
‘Miracle cure’ for spinal disorder rolled out on NHS – but babies still face paralysis – The Mirror March 19, 2023
Top 5 Most-Read Spinal Muscular Atrophy Stories of 2021 – AJMC.com Managed Markets Network December 26, 2021
As trials lag on Risdiplam's effectiveness in adults, the drug remains out of reach for many – ABC News December 10, 2021
NICE recommends risdiplam for spinal muscular atrophy – European Pharmaceutical Review December 6, 2021
Gene Therapy Improves Muscle Function for Children With Spinal Muscular Atrophy – Technology Networks December 1, 2021
Ideal Therapy Aids Motor Skills and Breathing, Taken Orally: UK Survey – SMA News Today November 3, 2021
Significant boost for children with Spinal Muscular Atrophy as new gene therapy is approved for use in Ireland – Irish Medical Times October 12, 2021
Babies with SMA able to swallow with Evrysdi® treatment – European Pharmaceutical Review September 26, 2021
‘It really is a miracle drug’: Yorkshire boy with spinal muscular atrophy receives ‘most expensive drug in the world’ at Sheffield Children’s Hospital – The Yorkshire Post September 21, 2021
Spinal Muscular Atrophy: Why An Early Diagnosis And Treatment Is Crucial For Patients – ABP Live September 15, 2021
New SMA Tracker Reveals Gaps in Access for People Living with SMA in Europe – EURACTIV PR September 7, 2021
Risdiplam improves motor function in infants with spinal muscular atrophy – Medical Xpress August 23, 2021
Spinal Muscular Atrophy awareness: Treatment advances offer hope to SMA patients – Firstpost August 15, 2021
7-year-old Bronx boy with Spinal Muscular Atrophy sworn in as NYPD officer for a day – WABC-TV July 29, 2021
The ‘most expensive drug in the world’, how it works and the devastating disease it treats – The Conversation UK July 21, 2021
Evrysdi approved in Japan for the treatment of spinal muscular atrophy – Spinal News International July 6, 2021
Gene therapy gives families hope for babies with spinal muscular atrophy – UNSW Newsroom July 2, 2021
