Improving Outcomes in Spinal Muscular Atrophy Through Early Identification and Personalization of Care – Neurology Live December 21, 2022
Paediatric patient with spinal muscular atrophy to get first gene therapy in BD – The Financial Express October 27, 2022
Improving Outcomes in Spinal Muscular Atrophy Through Early Identification and Personalization of Care – Neurology Live December 21, 2022
Paediatric patient with spinal muscular atrophy to get first gene therapy in BD – The Financial Express October 27, 2022
Should Treatment for Spinal Muscular Atrophy Be Initiated Earlier? – Neurology Advisor October 18, 2022
At a fashion show for people with spinal muscular atrophy, models take back their own stories – STAT September 20, 2022
Philadelphia girl with Spinal Muscular Atrophy beats odds, walks in fashion show ahead of New York Fashion Week – WPVI-TV August 31, 2022
Listing breakthrough brings hope for people with spinal condition – The Sydney Morning Herald August 18, 2022
FDA approves Roche's Evrysdi for use in babies under two months with spinal muscular atrophy (SMA) – StreetInsider June 3, 2022
University of Oxford: First UK pilot study of newborn screening for spinal muscular atrophy launched in Oxford – India Education Diary March 18, 2022
First UK pilot study of newborn screening for spinal muscular atrophy launched in Oxford – University of Oxford March 15, 2022
Emirati girl with spinal muscular atrophy takes her first few steps at Abu Dhabi long-term care hospital – Gulf News February 24, 2022
Baby given months to live may now outlive parents – after receiving world’s most expensive drug – National World February 8, 2022
£1.8m drug gives Cheshire baby a second chance at life after terminal diagnosis – Cheshire Live January 14, 2022
Top 5 Most-Read Spinal Muscular Atrophy Stories of 2021 – AJMC.com Managed Markets Network December 26, 2021
As trials lag on Risdiplam's effectiveness in adults, the drug remains out of reach for many – ABC News December 10, 2021
NICE recommends risdiplam for spinal muscular atrophy – European Pharmaceutical Review December 6, 2021