Muscular Dystrophy

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Rickmansworth turned orange to help support boy with muscular dystrophy – Watford Observer

Hundreds of people swapped their usual attire to dress head to toe in orange to raise £4,000…

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New drug for Duchenne muscular dystrophy clears phase 1 clinical trial testing in boys – Medical Xpress

Patients with Duchenne muscular dystrophy (DMD) have few treatment options. Medications currently available or in development either…

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Muscle wasting conditions: Transforming lives through research – Open Access Government

Catherine Woodhead, CEO, Muscular Dystrophy UK explains how lives are being transformed through research when it comes…

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Tips to Alleviate Symptoms of Constipation – Muscular Dystrophy News

Managing one’s health while living with a disability requires much more than regular trips to the doctor…

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Woman with muscular dystrophy creates clothing line to inspire others with chronic illnesses – ABC News

There was a time when 33-year-old Keisha Greaves hid her muscular dystrophy. Now, she embraces her condition…

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Finding the Perfect Wheelchair Blanket – Muscular Dystrophy News

Many YouTubers create meaningful content about their lives with disability and chronic illness. By showing what it’s…

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Who’s Moving: British Red Cross, Muscular Dystrophy UK, Pilotlight and more – Civil Society Media

Chief executive Muscular Dystrophy UK has appointed Catherine Woodhead as chief executive. She was previously director of development…

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Understanding a Rare Cancer in Duchenne Muscular Dystrophy Patients – Rare Disease Report

Muscle stem cells can contribute to a specific, rare cancer in patients with Duchenne muscular dystrophy (DMD),…

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Rickmansworth goes orange for muscular dystrophy – Watford Observer

An insurance broker is joining schoolchildren and school staff in wearing orange in a bid to raise…

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Duchenne muscular dystrophy (DMD): Correcting the dystrophin gene – Open Access Government

Dr Ahlke Heydemann, Associate Professor and Director of Medical School Curriculum at University of Illinois, Chicago explains…

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Researchers overcome hurdle in CRISPR gene editing for muscular dystrophy – Medical Xpress

The gene editing technique known as CRISPR is a revolutionary approach to treating inherited diseases. However, the…

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A researcher at BU works on a new drug for muscular dystrophy – Binghamton Homepage

A researcher at Binghamton University’s Pharmacy School is working on a new drug that could significantly prolong…

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Muscular dystrophy: ‘Try a bit harder to walk, daddy’ – BBC News

A man with muscular dystrophy has called for more psychological support for both him and his family. Andrew…

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Here’s How I Decorated My Wheelchair This Christmas – Muscular Dystrophy News

In my family, almost every holiday deserves decorations. Even Valentine’s Day is celebrated, with heart stickers on…

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Home-based pulmonary function monitoring for teens with Duchenne muscular dystrophy – News Medical

Heart and lung complications are responsible for much of the morbidity and mortality associated with Duchenne muscular…

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UMN researchers give new insight to muscular dystrophy patients – EurekAlert

New research by University of Minnesota scientists has revealed the three-dimensional structure of the DUX4 protein, which…

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Coping with Duchenne: Parents Swap Stories at ‘Futures’ Conference – Muscular Dystrophy News

Until her son, Will, was diagnosed with Duchenne muscular dystrophy as a 7-year-old, speech pathologist Tiffany Cook…

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Muscular Dystrophy UK to ramp up digital campaigning – Charity Digital News

Muscular Dystrophy UK is looking to expand its digital campaigning, including establishing an online campaigning network. The charity…

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Small Ways to Get in the Holiday Spirit – Muscular Dystrophy News

The holidays can be a tumultuous time. Advertisements would have us believe that the ups and downs…

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Living with Muscular Dystrophy – Muscular Dystrophy News

Muscular dystrophy refers to a group of genetic disorders associated with the progressive loss of muscle tissue…

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Muscular Dystrophy UK partnership to improve journeys for disabled road users – Open Access Government

A new partnership with charity Muscular Dystrophy UK (MDUK) will bring Changing Places accessible toilets to the…

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My Introduction to Medical Marijuana – Muscular Dystrophy News

Marijuana use in the United States dates back to the 1600s. Before being introduced as a recreational…

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Beach wheelchair helps 10-year-old get back to his ‘happy place’ – Stuff

Ten-year-old Thomas Morrison loves the water, but, until recently, going to the beach hasn’t been an option. Thomas…

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Here’s How I Host Parties While Still Caring for My Body – Muscular Dystrophy News

These days it’s more difficult than ever to hang out with my friends. They’re all working hard…

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Brothers Max and Jack go into business for muscular dystrophy research – The Advocate

Each week Max and Jack Butler create colourful artworks using a straw and food colouring as therapy…

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Wheelchair-accessible Halloween Happenings – Muscular Dystrophy News

Halloween pulls at my heartstrings. I love it so much that even Christmas comes in second. Maybe…

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The Simple Act of Opening a Door for Someone – Muscular Dystrophy News

Society is an odd concept if you really think about it. It controls us like puppets on…

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Promising new therapy spares muscle loss in Duchenne muscular dystrophy – Medical Xpress

A promising therapy for Duchenne muscular dystrophy (DMD) developed by University at Buffalo researchers is moving closer…

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A Girl’s Best Friend: Thoughts on Mobility Assistance Dogs – Muscular Dystrophy News

One of the best days of my life was when my family and I brought home my…

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A clothing line for women with chronic illnesses? Why 1 woman made it happen – Today.com

Keisha Greaves has always had a passion for fashion. So when she was diagnosed with limb-girdle muscular…

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Finding Doctors Who Understand Your Disease – Muscular Dystrophy News

In life, there are good and bad versions of everything. When it comes to doctors, some get…

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Gene-editing hope for muscular dystrophy – BBC News

Scientists have for the first time used gene-editing to treat Duchenne muscular dystrophy in a large mammal,…

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Boy With Muscular Dystrophy Gets Custom Star Wars-Inspired Wheelchair At StocktonCon – CBS Sacramento

It was a dream come true for a Stockton boy with a love for Star Wars. Linda…

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Seeing Both Sides of the Plastic Straw Controversy – Muscular Dystrophy News

A few years ago, if you had asked me what it means to be eco-friendly, I would…

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Families ‘heartbroken’ as rare illness drug rejected for NHS use – Shropshire Star

A charity has condemned a decision by health officials to reject a drug to treat a rare…

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Muscular Dystrophy UK cuts ties with Christine Hamilton over KKK tweet – Third Sector

The charity dropped its ambassador of five years over a tweet comparing the burka to outfits worn…

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OCD in Duchenne Muscular Dystrophy Features Distinct Phenotype, Associated Symptoms – Neurology Advisor

Obsessive compulsive disorder (OCD) is a somewhat prevalent psychiatric disorder in patients with Duchenne and Becker muscular…

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Family asked to prove son’s disability before boarding Jet2 flight – The Guardian

The family of a 10-year-old boy were asked to prove he had a disability before they were…

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Parenting as a DMD patient – pharmaphorum

Parenting as a DMD patient The sleepless nights and steep learning curve that will be familiar to any…

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Duchenne muscular dystrophy gene therapy trial put on hold – Genetic Literacy Project

Sarepta Therapeutics’ clinical trial for a gene therapy to treat Duchenne muscular dystrophy has been paused by…

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In Greece, One Family’s Struggle with Duchenne – Muscular Dystrophy News

In the mythology of ancient Greece, Hermes was the god of boundaries and transitions, with the ability…

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A new hope for muscular dystrophy patients – The Health Site

As per the joint study by InBody and Ipsos, 71 per cent of Indians suffer from poor…

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The amazing creations of a young artist with muscular dystrophy (Video) – Aleteia EN

At just 10 years old, this little girl has already had her work displayed in exhibitions. When she…

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How BBC reporter with muscular dystrophy helped Asos create a jumpsuit for people in a wheelchair – iNews

Fashion retailer Asos and sports reporter Chloe Ball-Hopkins, who has muscular dystrophy, have collaborated to make a…

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A dietary supplement increases muscle-force production by 50% in the Duchenne muscular dystrophy mouse model – Université Laval

A dietary supplement derived from glucose increases muscle-force production in the Duchenne muscular dystrophy (DMD) mouse model…

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Interacting with Kids Who’ve Never Been Around a Wheelchair – Muscular Dystrophy News

People can be downright rude when it comes to being around someone who’s different to them. You…

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What it’s like to find out your 6-year-old has incurable muscular dystrophy – Cambridge News

The parents of a little boy with a terminal genetic disorder are determined to help him live…

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Learning to Embrace Relapse with Muscular Dystrophy – Muscular Dystrophy News

Just eight years ago, a four-hour trip to Disneyland would barely touch me. I’d go on a…

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Dating with a Disability (Part 1) – Muscular Dystrophy News

Part one of a series. Last summer, I was looking through some BioNews Services articles when I came…

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Young man with Duchenne Muscular Dystrophy shares story of hope – WLWT Cincinnati

Anyone who has battled an illness, or went through a tough time in their life knows how…

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Upgrading the toolbox for Duchenne muscular dystrophy research with a new rabbit model – Science Daily

Scientists rely on the use of animal models to improve our understanding of lethal muscle-wasting disease Duchenne…

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Firefighters honored for campaign to cure muscular dystrophy – WMC Action News 5

The Memphis Fire Department’s Fill the Boot campaign kicks off in a few weeks. Monday, the city was…

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Charity runner to take on London Marathon for muscular dystrophy – Scottish Daily Record

A charity runner is taking on his most gruelling challenge yet to once again raise money for…

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Muscular Dystrophy Won’t Eclipse the Blessings of Everyday Life – Muscular Dystrophy News

Chronic illness can dramatically alter life perspective. If there’s anything I’ve learned from having mitochondrial myopathy, it’s…

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Breaking the Stigma of Asking for Help – Muscular Dystrophy News

A lot of people think that asking for help is a piece of cake. A walk in…

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Muscular Dystrophy wants Spinraza to be made available on the NHS – The National

DRUG bosses must approve a “lifeline” drug for use on the NHS to stop patients losing the…

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Genetic Compensation Mechanism Could Aid in Treatment of Muscle Disorders, Study Suggests – Muscular Dystrophy News

A genetic compensation mechanism discovered in zebra fish could have implications in the treatment of muscle diseases,…

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Codicote villagers rally round to support five-year-old with genetic disease – Welwyn Hatfield Times

Fundraising challenges and events are all being staged to support five-year-old William Eames, who was diagnosed with…

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Photos: Hip hop for muscular dystrophy – Sylvan Lake News

C.P. Blakely School students learned about muscular dystrophy today while also learning some sweet hip hop moves…

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Making My Bathroom Wheelchair-accessible – Muscular Dystrophy News

Renovating your home for wheelchair accessibility can seem like a daunting task. You would not be wrong….

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Call for ‘life-changing’ treatment to be approved in Scotland – The Scotsman

Patients with the most severe form of a genetic condition could lose the ability to move, breath…

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Research team helping better understand causes of muscular dystrophy – Medical Xpress

Using fruit flies, Texas A&M AgriLife Research scientists may be one step closer to better understanding the…

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Fitbit Is Not Just for the Able-bodied – Muscular Dystrophy News

Fitbits aren’t just for able-bodied fitness gurus; they have many more features than just counting footsteps. As…

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Charity ball and half marathon raise £5k for Muscular Dystrophy UK – Maidenhead Advertiser

Almost £40,000 has been raised for charity by one family over the last 34 years. During the last…

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Summit Therapeutics launches placing to raise £15mln to advance its treatment for Duchenne Muscular Dystrophy – Proactive Investors UK

Summit Therapeutics PLC (LON:SUMM) (NASDAQ: SMMT) has raised around £15mln from an accelerated book-build placing of 8,333,333…

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Young boy with muscular dystrophy steals the nation’s hearts on special edition of The Jeremy Kyle Show – Mirror.co.uk

On today’s episode of The Jeremy Kyle Show, brave young people were celebrated for the way they…

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Tamoxifen and raloxifene slow down the progression of muscular dystrophy – Science Daily

Steroids are currently the only available treatment to reduce the repetitive cycles of inflammation and disease progression…

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Can Genome Editing Improve the Outlook for Muscular Dystrophy? – Medical News Bulletin

Researchers investigate genome editing using CRISPR/Cas9 as a way to correct mutations related to Duchenne muscular dystrophy. Duchenne…

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Human ‘chimeric’ cells restore crucial protein in Duchenne muscular dystrophy – University of Illinois at Chicago

Cells made by fusing a normal human muscle cell with a muscle cell from a person with…

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Brave boy with muscle-wasting disease is determined to achieve his dreams – Express.co.uk

Draven Jefferies has Duchenne muscular dystrophy which will soon confine him to a wheelchair and could claim…

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Travelling with a disability: Meet the voyager who’s re-writing the rule book – The Telegraph

Angus Drummond was working in London in investment banking when he received the news that changed his…

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Patients living longer with Duchenne muscular dystrophy pose new challenge for caregivers – Science Daily

Diagnostic and treatment advances are helping patients with Duchenne muscular dystrophy — one of nine major types…

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Artist with muscular dystrophy to sell his work – East London and West Essex Guardian Series

A young artist with Duchenne muscular dystrophy is hoping to sell several pieces of art with all…

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UP: Muscular Dystrophy patients stage hunger strike seeking Centre’s assistance for treatment – Business Standard

A mother-daughter duo suffering from Muscular Dystrophy embarked on a hunger strike demanding assistance from the Centre…

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What I Use to Prevent Neck Pain – Muscular Dystrophy News

I’ve had bad posture my entire life. Growing up, I didn’t know why I always slouched so…

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Havering teen with Muscular Dystrophy hoping to sell his ‘incredible’ artwork in support of Haven House Children’s Hospice – Yellow Advertising – Havering

A HAVERING teen with Muscular Dystrophy is hoping to sell his ’incredible’ artwork in support of Haven…

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This Small Molecule Protects the Muscles of Patients With Duchenne Muscular Dystrophy – Labiotech.eu

Summit Therapeutics’ treatment for the devastating disease, Duchenne muscular dystrophy, reduces inflammation, which could protect muscle fibers…

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How to Buy a Wheelchair-accessible Van – Muscular Dystrophy News

For the first couple years of having mitochondrial myopathy, I used a manual wheelchair to get around….

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Firefighters raise the roof for muscular dystrophy – Spruce Grove Examiner

If you’ve taken a drive down King Street over the last few days, you may have noticed…

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Growing Thicker Skin – Muscular Dystrophy News

It’s inevitable that people will treat you different when you’re in a wheelchair, whether that works in…

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A UK charity has urged Twitter to do more to stop abuse of disabled users – BT.com

A charity has urged Twitter to do more to help disabled users report hate speech against them…

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What Is Oculopharyngeal Muscular Dystrophy (OPMD)? – Muscular Dystrophy News

Oculopharyngeal muscular dystrophy (OPMD) is a genetic disease that is characterized by muscle wasting. As its name…

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Gene Therapy in Muscular Dystrophy – Muscular Dystrophy News

Gene therapy, the use of genetic material to treat a disease or disorder, is making strides in…

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Brave Leo inspires major muscular dystrophy fundraising drive – The Inverness Courier

BATTLING parents of a brave Inverness three-year-old are set to launch a fundraising drive towards research into…

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AI trial to help accelerate future treatments for Duchenne muscular dystrophy – Imperial College London

The Duchenne Research Fund has granted 320,000 pounds to Imperial experts, who hope to help doctors make…

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Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing – Science Advances

Abstract Genome editing with CRISPR/Cas9 is a promising new approach for correcting or mitigating disease-causing mutations. Duchenne muscular…

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Brave Alec gets to make his own Lego movie – The Yorkshire Post

Alec Syphas suffers muscular dystrophy and wanted to make a Lego movie. Catherine Scott reports. An eight…

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Parents of Irish boy with Duchenne Muscular Dystrophy in race against time to secure life-changing medication – The Irish Sun

THE parents of a young boy with Duchenne Muscular Dystrophy face a race against time to secure…

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Stem cell therapy, a new hope to fight against Muscular Dystrophy & other Neurological Disorders – E-Pao.net

Nerul Navi Mumbai based, NeuroGen Brain and Spine Institute, which is India’s leading stem cell therapy cum…

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Scammers clear out terminally ill Antrim boy’s holiday fund – Belfast Telegraph

A dream holiday for a terminally ill little boy will go ahead – despite heartless scammers clearing…

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Disabled taxi price premium condemned by charity – BBC News

Confusion over new rules for disabled taxi passenger fares has led to “discriminatory” price differences, a charity…

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Teen with muscular dystrophy speaks out after travel struggles at Charlotte airport – WBTV

Lori Watkins and her 15-year-old son, Seph Ware, claim they have traveled from their home in Lynchburg,…

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£415 raised for Muscular Dystrophy UK – Cambrian News

Madam Following the closure of the Muscular Dystrophy shop on Bath Street, Aberystwyth, the volunteers have been busy fundraising. On Friday, 8 December, a very…

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Improved Outcomes in Duchenne Muscular Dystrophy With Long-Term Glucocorticoid Treatment – Neurology Advisor

Lifelong use of glucocorticoids is associated with physical strength and function improvements, greater health-related quality of life, and improved survival in patients with…

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Reprogrammed Stem Cells Regenerate Muscle In Muscular Dystrophy – ReliaWire

Human mesodermal induced pluripotent stem cell derived progenitors can successfully engraft into the skeletal muscle and hearts of dystrophic mice, researchers from Northwestern…

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Scientists Reprogram Stem Cells to Regenerate Muscle in Muscular Dystrophy – Northwestern University NewsCenter

Specially programmed stem cells demonstrated the potential to regenerate lost muscle mass in muscular dystrophy, according to a Northwestern Medicine study published in…

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Biotech startup Myonexus raises funds for clinical trial of muscular-dystrophy gene therapy – The Columbus Dispatch

Biotechnology company Myonexus Therapeutics has raised $2.5 million in financing from CincyTech, Rev1 Ventures, the Jain Foundation and GFB ONLUS, which joined existing…

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Staying Warm Even when It’s Rough Outside – Muscular Dystrophy News

When people ask me what my favorite season is I always say winter. I find that it’s much easier to warm up your…

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Duchenne muscular dystrophy: new drug promises better medication – The Health Site

Researchers have found a new drug that reduces fibrosis (scarring) and prevents loss of muscle function in an animal model of Duchenne muscular…

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Scientists slow progression of fatal form of muscular dystrophy – Science Daily

In a paper published in the Nature journal Scientific Reports, Saint Louis University (SLU) researchers report that a new drug reduces fibrosis (scarring)…

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Friends hold disco for boy with muscular dystrophy – North Somerset Times

Laura Bindon and her friends raised £1,558 with a disco at the Ring O’Bells in support of Luke’s Army. The charity has been set…

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Aylesbury 11-year-old gets prestigious scout award – Mix 96

Disabled Boy gets Prestigious Scout Award An 11-year-old boy from Aylesbury who has a rare disability has been awarded a prestigious scouting award. Callum Smith…

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Researchers Devise Improved Gene-Editing Process for Duchenne Muscular Dystrophy – UT Southwestern Medical Centre

Gene-editing Developed & Improved For Duchenne Muscular Dystrophy Researchers at the UT Southwestern Medical Centre have developed an improved and simplified gene-editing. The technique…

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Couple receive Lifetime Achievement award from Muscular Dystrophy UK after decades of fundraising efforts – Scottish Daily Record

A Whitburn couple have been given a Lifetime Achievement award for their dedication to raising awareness of muscle-wasting conditions. Jeff and Joan Wight devoted…

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Glucocorticoids offer long-term benefits for patients with Duchenne muscular dystrophy – Medical Xpress

Glucocorticoids, a class of steroid hormone medications often prescribed to patients with Duchenne muscular dystrophy (DMD), offer long-term benefits for this disease, including…

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Families in limbo after FDA rejection of new drug for muscular dystrophy – Daily Globe

Ashley Rassett and Roberto Enriquez want to give their son a fighting chance. The Woodbury couple’s 3-year-old son Gian was recently diagnosed with Duchenne…

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How to Maintain Your Hobbies – Muscular Dystrophy News

I’ve been drawing and sketching ever since I could pick up a marker. For me, drawing isn’t just a hobby or a way…

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Significant Improvements Reported in Duchenne Muscular Dystrophy Patients Treated with Capricor’s Investigational Cell Therapy – PR Newswire

Boys and young men in advanced stages of Duchenne muscular dystrophy experienced significant and sustained improvements in cardiac structure and function, as well…

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Disabled motor racing fan in the driving seat thanks to £15,000 powered wheelchair appeal – Leicester Mercury

A teenage motor racing fan with muscular dystrophy is the proud owner of a “top of the range” powered wheelchair thanks to a…

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Duchenne muscular dystrophy sufferers cannot walk – Daily Mail

Two brothers suffering the same debilitating disorder face a greater risk of muscle deterioration and early death after the US Food and Drug…

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Man with muscular dystrophy finishes 3-year sailing trip – Fox 5 San Diego

A San Diego man was diagnosed with muscular dystrophy in his early twenties. Instead of giving in to the degenerative disease, he decided…

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FDA declines to approve PTC’s Duchenne Muscular Dystrophy drug – Nasdaq

The U.S. Food and Drug Administration has declined to approve PTC Therapeutics Inc’s experimental drug to treat Duchenne muscular dystrophy, saying an additional…

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Music was his ‘saviour’ when kid with muscular dystrophy couldn’t fit in – TODAY Online

Sheikh Mohd Danial Bawthan was 14 when he started to feel the impact of how different he was from his peers. “My friends would…

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Mum and son grateful for charity run support – Cambrian News

A LLANGEITHO mother has raised over £1,500 for muscular dystrophy after completing the Cardiff Half-marathon to help raise money and awareness for the…

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Runners tough it out in support of Muscular Dystrophy UK – Weston & Somerset Mercury

The Two Bays Tough Ten Challenge returns to Weston in 2018 and will once again be supporting Muscular Dystrophy UK as its race…

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Charity events: Muscular Dystrophy Association Comedy Fundraiser, Art With a Heart for Children – Akron Beacon Journal

This Week Wednesday Muscular Dystrophy Association Comedy Fundraiser — 8 p.m. at Funny Stop Comedy Club, 1757 State Road, Cuyahoga Falls. $15. Featuring Basile. 330-923-4700. Friday Art…

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Bionano Genome Mapping Superior for Identifying Structural Variants in Duchenne Muscular Dystrophy – Technology Networks

In a publication in Genome Medicine, a team of researchers from Children’s National Health System(CNHS) and the University of California, Los Angeles (UCLA)…

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Graduate With Muscular Dystrophy Gets His Dream Disney Trip – Muscular Dystrophy News

According to The Morning Call, 23-year-old DeSales University graduate Derek Szena who has muscular dystrophy desperately wanted to visit Disney World, but the…

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Grandmother Christine Ogden arranges concert to raise roof for Muscular Dystrophy UK – The Bolton News

A GRANDMOTHER is hoping to raise more than £8,000 for a cause close to her heart. For the thirteenth year in a row Christine…

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3-Year-Old MD Patient Completes Half-Marathon With His Dad – Muscular Dystrophy News

Most 3-year-olds only get to watch marathons from the sidelines or on television, but not Levi Gagner. The Rare Disease Report…

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5 Tips for Emotionally Coping With Duchenne Muscular Dystrophy – Muscular Dystrophy News

As boys with Duchenne muscular dystrophy get older, their disease progresses and it’s likely that their emotional response to the disease will change…

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Animated Film Helps Explain Duchenne Muscular Dystrophy to Kids – Muscular Dystrophy News

In this animated video from the Parent Project Muscular Dystrophy, Tim and Moby talk about Duchenne muscular dystrophy in a way that children…

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Risk factors for Duchenne muscular dystrophy identified – UT Southwestern Medical Center

A new study from UT Southwestern suggests that more people with Duchenne muscular dystrophy could live longer by identifying and more aggressively treating…

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C-Path and CDISC announce therapeutic area user guide for Duchenne Muscular Dystrophy – Medical Xpress

Critical Path Institute (C-Path) and The Clinical Data Interchange Standards Consortium (CDISC) announce the open availability of a Duchenne Muscular Dystrophy Therapeutic Area…

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Charity shop closes its doors after 31 years – Cambrian News

A WOMAN who founded an Aberystwyth charity shop after her four children were diagnosed with a rare genetic disease has shut up shop…

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Chronic inflammation plays critical role in sustained delivery of new muscular dystrophy therapy – Medical Xpress

Macrophages, a type of white blood cell involved in inflammation, readily take up a newly approved medication for Duchenne muscular dystrophy (DMD) and…

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Jacob Jarvis shares about his battle against Duchenne’s Muscular Dystrophy – Fox 28

17-year-old Jacob Jarvis appeared on Good Day Columbus to share about his battle against Duchenne Muscular Dystrophy Friday. Jarvis has been battling the disease…

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Muscular Dystrophy: Heartbroken Family Awaits FDA Decision on Experimental Drug – Newsweek

Max, Rowan and Charlie Vertin’s muscles have been slowly collecting damage since the day they were born. Someday, they will not be able…

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Duchenne Muscular Dystrophy boy’s ‘huge strides’ after Manx NHS U-turn – BBC News

An eight-year-old boy with a rare muscle-wasting disease is “making huge strides” after the Manx NHS reversed its decision not to fund his…

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Helpers rally for Milton brothers with Duchenne muscular dystrophy – The Daily Gazette

With a few extra feet of floor space, Alex and Tina Frolish will finally be able to stop manually lifting their teenage sons…

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Sarepta shines spotlight on next-gen muscular dystrophy drug – FierceBiotech

Controversy over data quality took the shine off Sarepta’s U.S. approval of Duchenne muscular dystrophy drug Exondys51 last year. Now the company is…

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‘CRISPR-Gold’ repairs muscular dystrophy gene in mouse model – BioNews

Scientists have repaired the faulty gene in a mouse model of muscular dystrophy by using gold nanoparticles to deliver the genome editing tool…

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Kielder mum running to help sons beat muscle-wasting condition – Northumberland Gazette

A mother-of-two is preparing to take on the Kielder 10k run tomorrow to raise funds towards a treatment that could help her sons….

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Opportunities at the Muscular Dystrophy Association – Muscular Dystrophy News

The Muscular Dystrophy Association (MDA) is the largest organization in the U.S. dedicated to helping children and adults with muscular dystrophy…

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Politicians urged to seek deal on Muscular Dystrophy drug – The Irish Times

A group campaigning for access to treatment for young boys with Duchenne Muscular Dystrophy has pleaded with the Health Service Executive (HSE) and…

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Helpful Tips for Independent Living With a Personal Care Assistant – Muscular Dystrophy News

Independent living can be achievable for many adults with muscular dystrophy (MD), but there are various factors to consider to ensure you get…

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Muscular Dystrophy UK store in South Woodham Ferrers to close – Chelmsford Weekly News

A charity store which has raised funds for Muscular Dystrophy for the past 21 years is changing charity. The shop, in South Woodham Ferrers,…

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Southampton mum hosting ball to help fight muscular dystrophy – Daily Echo

A SOUTHAMPTON mum is holding a charity ball to help fight muscular dystrophy, after her daughter was born with the condition. Sian Rixon helped…

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Restoring breathing capacity in Duchenne muscular dystrophy by activating the brain – Science Daily

New research published in The Journal of Physiology today suggests that enhancing breathing via the brain may limit deficiencies in respiratory capacity in…

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Family raises money for muscular dystrophy charity at Maidenhead United game – Windsor Express

A family of three from Shurlock Row raised money and awareness about muscular dystrophy at a Magpies game on Saturday. Dean Yorke was diagnosed…

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7 Myths About Physical Therapy – Muscular Dystrophy News

Muscular dystrophy (MD) is a neuromuscular disorder, characterized mainly by progressive muscle loss. Physical therapy plays an important role in MD treatment, however,…

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Ramblers set to raise funds for muscular dystrophy – The Gazette

A GROUP of ramblers are heading in the right direction to raise funds and awareness of a debilitating illness. Mairi Leitch, 34, from Lochwinnoch…

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Henlow youngsters’ fun day raises more than £2600 for Muscular Dystrophy UK – Comet 24

The 15 young people from the National Citizen Service had live music, bouncy castles, a penalty shootout and much more at the Henlow…

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‘Coach to Cure MD’ and Other Fundraising Events Mark Duchenne Muscular Dystrophy Month – Muscular Dystrophy News

For the ninth year in a row, “Coach to Cure MD” and Parent Project Muscular Dystrophy (PPMD) will mark Duchenne Awareness Month by…

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Scientists discover ‘internal clock’ inside human cells – paving the way to understanding diseases like muscular dystrophy and cancer – Daily Mail

Researchers have discovered the ‘internal clock’ of cells – breaking new ground to understand how diseases take hold of the body. Previously, the biological…

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Shortened Telomeres Linked to Dysfunction in Duchenne Muscular Dystrophy – Technology Networks

Researchers from the Perelman School of Medicine at the University of Pennsylvania have made a discovery about muscular dystrophy disorders that suggest new…

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Housing staff step out for Muscular Dystrophy charity – North Wales Chronicle

MORE than 20 members of staff working for the largest housing association in north Wales stepped out to raise £1250 to help people…

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MRI Spots Progression of Facioscapulohumeral Muscular Dystrophy Better Than Standard Methods, Study Reports – Muscular Dystrophy News

MRIs can pick up subtle muscle changes that standard tests cannot in slowly progressing disorders such as facioscapulohumeral muscular dystrophy, or FSHD, a…

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His telethons were as famous as his movies: How comedy legend Jerry Lewis raised over $2billion for muscular dystrophy over 45 years with his 21-and-a-half hour Labor Day spectaculars – Daily Mail

Jerry Lewis went down in history not only as a legendary comedian, but a hero to individuals around the world combating muscular dystrophy…

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Why I Drink Gatorade – Muscular Dystrophy News

In 1965, a coach for the University of Florida football team — the Gators — noticed that his players were being affected by…

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Inspirational story: Chinese teen with muscular dystrophy admitted to college – CCTV

A Chinese teen who was diagnosed with progressive muscular dystrophy at the age of one has been admitted to Hangzhou Dianzi University because…

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Jerry Lewis raised billions to fight Muscular Dystrophy with his groundbreaking telethons – The Sun

JERRY Lewis raised over £1.95BILLION to fight Muscular Dystrophy through his groundbreaking telethon fundraisers. The iconic comedian has died aged 91. Throughout his lengthy career,…

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4-year-old girl with rare form of muscular dystrophy returns home from hospital for the first time – ITV News

A four-year-old girl who has a rare form of muscular dystrophy has returned home to live for the first time after spending her…

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Gene therapy reverses muscular dystrophy in dogs in world first – BioNews

A safe and effective gene therapy treating Duchenne muscular dystrophy (DMD) in dogs has been demonstrated by researchers from France and the UK. The…

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Monmouthshire taxis not ready to meet disabled legislation – Abergavenny Chronicle

Disabled taxi users in Monmouthshire won’t be able to take advantage of a new law aimed at giving them accessibility and fare parity…

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Wheelchair users ignored by Warwick District Council – Stratford Observer

PEOPLE with disabilities in Warwick district will not be protected by a new law ensuring equal treatment for taxi users. A change in the…

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Taxi drivers in Bury ‘can discriminate with impunity’ against disabled – Bury Times

BURY Council has no plans in place to deal with a law change supporting disabled taxi users, it has been revealed. A change in…

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New test for screening of Duchenne muscular dystrophy in newborn babies – Medical Xpress

Researchers at Cardiff University and Cardiff and Vale University Health Board have developed a more reliable method of screening for Duchenne muscular dystrophy…

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My Walk with Faith While Living with MD – Muscular Dystrophy News

People are always surprised at how faithful my family is. They think that because of my illness we would automatically throw our faith…

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7 Common Early Symptoms of Duchenne Muscular Dystrophy – Muscular Dystrophy News

Duchenne muscular dystrophy (DMD) is a genetic disease that causes muscles to progressively weaken. The condition affects mainly boys and the onset of…

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Gene therapy reverses muscular dystrophy symptoms in dogs – Digital Trends

As difficult as it is when our beloved pet dogs get old, it’s a whole lot worse if their decline is the result…

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Novel therapeutic advances for muscular dystrophy, spinal muscular atrophy – AAP News

Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) are neuromuscular diseases with early onset, progressive weakness and previously without mutation-specific therapies. This…

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Children with muscular dystrophy will not get new drug – The Irish Times

A new treatment for children with Duchenne muscular dystrophy will not be made available in the Republic, the Health Service Executive has decided. Muscular…

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Gene transfer corrects severe muscle defects in mice with Duchenne muscular dystrophy – Science Daily

Duchenne muscular dystrophy is a rapidly progressive disease that causes whole-body muscle weakness and atrophy due to deficiency in a protein called dystrophin….

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Gene therapy: Microdystrophin restores muscle strength in Duchenne muscular dystrophy – Science Daily

Researchers from Genethon, the AFM-Telethon laboratory, Inserm (UMR 1089, Nantes) and the University of London (Royal Holloway) demonstrated the efficacy of an innovative…

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Fresh hope for muscular dystrophy sufferers – The Scotsman

A single jab for muscular dystrophy developed by British scientists has the potential to help those with the illness, a professor has said. A…

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Hope for children with muscular dystrophy after scientists restore muscle strength in dogs – Telegraph.co.uk

Children with the most common form of muscular dystrophy have been offered hope of living a healthy life after a breakthrough gene therapy…

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Davenport parents say experimental drug helps son with severe form of muscular dystrophy – News Chief

Like a typical younger sibling, Benjamin Rodriguez, 4, hovers around his brother, Derek, eager to share in what he is doing. Derek, 8, kneels…

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Cononley woman with muscular dystrophy to kayak for two miles along Leeds and Liverpool Canal – Craven Herald

A WOMAN from Cononley who has a form of the illness muscular dystrophy will take to the water this weekend to raise cash…

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Who is Nikki Fox? Watchdog Live presenter and award-winning reporter who has muscular dystrophy – The Sun

WATCHDOG Live has returned, which means presenter Nikki Fox is back on our screens. But who exactly is the award-winning journalist? Here’s all you…

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6 Complications of Muscular Dystrophy – Muscular Dystrophy News

Muscular dystrophy (MD) is a progressive disease that causes muscle weakness and loss of muscle mass. There are many different types of muscular…

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Firefighters hold shooting competition for muscular dystrophy – NTV

Firefighters in Grand Island were strapping up for a good cause on Saturday. They held their first-ever muscular dystrophy charity shoot to raise funds…

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Helicopter company gives boy with muscular dystrophy a boost – The Oxford Times

A YOUNG boy with muscular dystrophy will see his Witney home adapted to help him move around thanks to a donation of nearly…

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Disabled Hornchurch man calls for others to make most of multi-million pound programme – Romford Recorder

Jack McLellan, 25, from Hornchurch, has an undiagnosed form of muscular dystrophy and knows first hand how difficult it can be to find…

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Heartbreak of North Shields family whose seven-year-old son ‘could be in a wheelchair by age of 12’ – Chronicle Live

A horrific muscle-wasting condition could leave this little boy in a wheelchair by the age of 12. Ty Coates has Duchenne Muscular Dystrophy, which…

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Designed proteins to treat muscular dystrophy – Science Daily

This is a cross section of a muscle biopsy: Blood vessels (red) between…

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How inspirational student Jordan Clements defied muscular dystrophy to realise his lifelong dream of being a doctor – Belfast Telegraph

Medical graduate Jordan Clements has completed one of the toughest degrees at Queen’s despite suffering from muscular dystrophy – all inspired by a…

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6 of the Best Apps for Chronic Illness Management – Muscular Dystrophy News

Managing a chronic illness can be difficult. There are many different medications to take (often at different times), appointments to remember, symptoms to…

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Appeal to renovate disabled Rugby boy’s home – Rugby Advertiser

Friends of a Rugby family with a disabled 11-year-old son are appealing to the community to help renovate their home to make it…

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Swiss Scientists Have Designed New Proteins to Treat Muscular Dystrophy – Labiotech.eu

Researchers at the University of Basel have designed two proteins that can reverse congenital muscular dystrophy and increase the lifespan of mice. Congenital muscular…

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Disabled patients ‘relying on crowdfunding’ for wheelchairs – The Guardian

Disabled patients are increasingly having to rely on crowdfunding to pay for wheelchairs, a leading doctor has warned. Cuts in services, a postcode…

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The Importance of Speech-Language Pathologists for Neuromuscular Disorder Patients – Muscular Dystrophy News

Speech-language pathologists (SLPs) or speech-language therapists (SLTs) do much more than help people with speech problems such as stuttering or mispronouncing words. For…

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Simultaneously Inhibiting Three Proteins Can Increase Muscle Mass in Mice with Muscular Dystrophy, Study Shows – Muscular Dystrophy News

Simultaneously inhibiting three proteins can increase muscle mass, a finding that could help those with diseases such as muscular dystrophy and cancer that…

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Researchers aim to repurpose former experimental cancer therapy to treat muscular dystrophy – National Institutes of Health

Diaphragm muscle from SU9516 treated dystrophin deficient mouse showing nuclei (blue), myofibers (outlined…

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Muscle growth finding may assist with cancer treatment – Monash University

Monash University’s Biomedicine…

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Radcliffe mother’s appeal for better support for disabled children after being left with logistical nightmare – Bury Times

A SINGLE-PARENT who has a son with an incurable muscle wasting condition has called for better support for disabled children after being left…

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4 Things to Know About Using Medicinal Marijuana – Muscular Dystrophy News

Using cannabis or marijuana for medicinal purposes is a hot topic right now among patients and health practitioners. It’s regularly touted as a…

0854

Kids ask wheelchair-bound muscular dystrophy sufferer intimate questions about his life, his illness, and even his dating habits in a heart-warming video – Daily Mail

Having a conversation about disease and disability can be a sensitive difficult task for everyone involved. So who better to help us learn…

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MoveDMD Study Continuing to Progress, Catabasis CEO Says in Interview – Muscular Dystrophy News

MoveDMD (NCT02439216) is a three-part, ongoing clinical trial investigating an oral drug — edasalonexent (CAT-1004) — as a potential…

0851

Talking to Family Members About Your Child’s Neuromuscular Disorder – Muscular Dystrophy News

A neuromuscular disorder diagnosis will have a profound effect on the whole family. Younger siblings often don’t fully understand what a neuromuscular disorder…

0851

Disability accessibility, acceptance and how a country community is helping James go places – ABC Online

Without a roadworthy vehicle, James Baxter-O’Shea has limited accessibility and spends much of his day sitting at home in front of a computer…

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Weekly steroids strengthen, repair muscles – Science Daily

Weekly doses of glucocorticoid steroids, such as prednisone, help speed recovery in muscle injuries, reports a new Northwestern Medicine study. The weekly steroids…

0871

Timothy Stoklosa, gifted artist who battled Duchenne muscular dystrophy, dies at 33 – Press Herald

Timothy Stoklosa, a gifted artist who battled Duchenne muscular dystrophy, died on May 12. He was 33. Stoklosa worked as art director at The…

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How Service Dogs Can Benefit People With Neuromuscular Diseases – Muscular Dystrophy News

Service dogs are typically thought of as necessary companions for the visually impaired, but service and therapy dogs can be incredibly helpful for…

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Weekly Instead of Daily Steroids May Prevent Muscular Dystrophy Muscle Wasting, Study Reports – Muscular Dystrophy News

Using glucocorticoid steroids once a week instead of once a day to slow the progression of muscular dystrophy (MD) could prevent downsides of…

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How to Talk to Your Child About Their Neuromuscular Disorder – Muscular Dystrophy News

Finding out your child has a neuromuscular disorder is an incredibly difficult time for the whole family, but you adjust quickly. While your…

0871

The Importance of Respiratory Care for Muscular Dystrophy – Muscular Dystrophy News

Respiratory care is an important element of care for muscular dystrophy (MD) patients. As the disease progresses, the muscles required to breathe and…

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Mum raises thousands to help fund a cure for her daughter – Barrhead News

THE family of a 12-year-old girl who has one of the rarest forms of Muscular Dystrophy have raised thousands to help find a…

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5 Tips to Help Prevent Lung Infections – Muscular Dystrophy News

Muscular dystrophy (MD) patients are susceptible to lung infections which can often lead to hospitalization. According to the American Lung Association,…

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Duchenne Muscular Dystrophy – Cost of Care High, Quality of Studies Low – Rare Disease Report

A systematic review of 58 studies involving Duchenne muscular dystrophy (DMD) by Leadley et al in the Orphanet Journal…

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Maidenhead Community Centre hosts fundraising day for Muscular Dystrophy UK – Maidenhead Advertiser

More than…

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7 Physical Clues You Could Have Depression – Muscular Dystrophy News

Many people who suffer from chronic illnesses also suffer from depression. Depression isn’t something that should be overlooked; it should be brought to…

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Adam Sevenoaks, who suffers with Muscular Dystrophy, was asked to be the team mascot for Chickerell Under 13s Football Club – Dorset Echo

TEAM MASCOT: Adam and Mary Sevenoakes with manager Chris Evans, left, and assistant…

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5 Ways to Help Fund SMA and Muscular Dystrophy Charities – Muscular Dystrophy News

Non-profit organizations for spinal muscular atrophy (SMA) and muscular dystrophy are reliant on help from people to raise both funds and…

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Gene-editing alternative corrects Duchenne muscular dystrophy – Science Daily

Image shows heart muscle that is missing the dystrophin molecule.Credit: UT…

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What a Doctor Wants People to Know About Chronic Illnesses – Muscular Dystrophy News

Having a chronic illness presents many challenges for patients, not only in terms of managing the symptoms they suffer but also having to…

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Gene-editing alternative corrects Duchenne muscular dystrophy – UT Southwestern Medical Center

DALLAS – April 12, 2017 – Using the new gene-editing enzyme CRISPR-Cpf1, researchers at UT Southwestern Medical Center have successfully corrected Duchenne muscular…

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Researchers Identify Protein with Crucial Role in Muscle Formation – Muscular Dystrophy News

A small protein called Myomixer plays a crucial role in the development of skeletal muscle, the type of muscles the body uses to…

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Disability benefit changes ‘compromising people’s independence’ – East Lothian Courier

More than 50,000 disabled people have had specially adapted cars and other vehicles taken away as they move over to a controversial new…

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Wheelchair user asked to make space pram with a doll – Metro

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Incremental clinical advances for Duchenne Muscular Dystrophy – Managed Healthcare Executive

Duchenne Muscular Dystrophy (DMD) is a progressive disease that strikes young boys. It is universally fatal, but advances in the understanding of its…

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Long distance bicyclist rides through Kingman bringing awareness for muscular dystrophy – Kdminer

KINGMAN – Long distance bicyclist T.J. Forrester rode through Kingman Wednesday to raise awareness for muscular dystrophy. Having traveled 7,300 miles, Forrester is half…

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Woman Invents Magnetic Shirt to Help People With Disabilities – Muscular Dystrophy News

Following her husband’s frustration at not being able to do up the buttons on his formal work shirts, Maura Horton came up with…

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The heartwarming moment a young girl with muscular dystrophy achieves her ‘biggest dream ever’ to dance with the Australian Ballet Company – Daily Mail

A young girl from Victoria with a crippling illness which limits her movement has been able to achieve her dream of being a…

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Tributes paid to award winning Muscular Dystrophy UK volunteer Nancy – Solihull Observer

An AWARD-winning charity volunteer who dedicated over…

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Fill the Boots for muscular dystrophy – Virden Empire Advance

Firefighters camp out on Tim Horton’s roof “We are doing a roof-top campout for Muscular…

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Muscular Dystrophy Focus of $7M in Grants for 29 Research Projects – Muscular Dystrophy News

The Muscular Dystrophy Association (MDA) has awarded $7 million in grants to 29 top researchers for projects it says will potentially…

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National charity accuses Bradford hospitals chiefs of failing to do enough for patients with muscular dystrophy – Bradford Telegraph and Argus

HEALTH campaigners have accused Bradford Teaching Hospitals NHS Foundation Trust of ignoring calls to invest in expert care for people with muscular dystrophy. National…

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Inspirational schoolgirl with limb girdle Muscular Dystrophy raises £7200 for charity – Leicester Mercury

Jessica Blacknell, 10, from Leicester, was told in November that she has…

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Genetic study identifies new type of muscular dystrophy – BioNews

Scientists have identified a unique form of congenital muscular dystrophy (MD), characterised by short stature, intellectual disabilities and cataracts. The disorder, which shares symptoms…

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Winnipeg firefighters camp on roof for Muscular Dystrophy Canada – CBC.ca

The five firefighters who have been camping on top of the Osborne Village Fire Hall for Muscular Dystrophy Canada since Tuesday have experienced…

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Man with muscular dystrophy to travel through Europe as ‘human … – WNCN

An Indiana man with muscular dystrophy will travel through Europe strapped to his friends’ backs as a “human backpack”. Read…

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‘Teen Mom’ Leah & Corey’s Daughter Ali Still Walking Despite Doctors’ Doubts – RadarOnline

Teen Mom 2 star Leah Messer and her ex-husband Corey Simms’ daughter Ali may fall five times a day as a result of…

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Orem boy with muscular dystrophy in the running to win $5K adaptive bike – Daily Herald

Devin Sundquist, 12, third from right, and his stepfather Jared Stahura, fourth from left, pose for a photo with the staff of a…

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IN PICTURES: 10-year-old with muscular dystrophy among those making a splash in charity swimathon – Warrington Guardian

A GROUP including a 10-year-old with muscular dystrophy completed a charity swimathon at the weekend. Swimmers from across the town took part in…

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‘Town and Gown run will help us beat muscular dystrophy’ – The Oxford Times

A SCIENTIST who has spent his life trying to find a cure for muscular dystrophy is backing this year’s Town and Gown fundraising…

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End of the road for South West Wales Muscular Dystrophy group after five decades of fundraising – South Wales Evening Post

IT started with a letter in the South Wales Evening Post half a century ago — but now time is being called on…

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Heart Tissue Regeneration Study in Zebrafish Looks to Trigger Muscle Repair in People – Muscular Dystrophy News

The findings, published in the journal Development, might lead the way to drugs that help the body build new muscle cells, a crucial…

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Eugene tattoo artist takes part in national muscular dystrophy fundraiser – KVAL

This time of year, the Muscular Dystrophy Association sells thousands of paper shamrocks across the nation, hoping to raise money for research, treatment,…

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New Award Will Advance Muscular Dystrophy Research – University of Rochester Newsroom

University of Rochester Medical Center (URMC) neurologist Charles Thornton, M.D. has received a Javits Neuroscience Investigator Award from the National Institutes of Health…

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FDA rejects new drugs for Duchenne muscular dystrophy – San Francisco Chronicle

It starts with a loss of muscle function that worsens over time and eventually leads to problems with the heart and lungs. Approximately…

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Airdrie firefighters fight Muscular Dystrophy – Calgary Sun

Airdrie firefighters Three Airdrie firefighters spent 72 hours on the roof of Airdrie’s Boston Pizza, collecting $11,535 for Muscular Dystrophy Canada. Mattamy Homes…

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In Diagnosing Muscular Dystrophies, Review Finds MRI Analysis to Be Best Overall Approach – Muscular Dystrophy News

Ultrasound is typically used to study muscle thickness, and can identify both atrophic changes and fatty degeneration — particularly useful in the diagnosis…

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Search for Specific Myotonic Dystrophy Biomarkers Unsuccessful, According to Spanish Study – Muscular Dystrophy News

Myotonic dystrophy is a genetic disease caused by changes in the DMPK gene. Symptoms include muscular, heart, and psychological problems. However, there is…

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Muscular Dystrophy Treatments May Benefit from Fetal Muscle Stem Cells’ Increased Capacity to Regenerate – Muscular Dystrophy News

“These results help explain the differences between the capacity of fetal and adult muscle stem cells to repair muscle. Such an understanding is…

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European Journal of Human Genetics advance online publication 2 March 2016; doi: 10.1038/ejhg.2016.16 – Nature.com

Muscular dystrophies (MD) are a clinically and genetically heterogeneous group of Mendelian diseases. The underlying pathophysiology and phenotypic variability in each form are…

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Montreal brothers with muscular dystrophy hope to inspire with new album – Globalnews.ca

The Tshuma brothers were born in Zimbabwe and both suffer from muscular dystrophy, an incurable disease that causes progressive weakness and loss of…

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MDA Shamrocks Help Fight Muscular Dystrophy – PR Newswire (press release)

CHICAGO, March 1, 2016 /PRNewswire-USNewswire/ — Tens of thousands of retailers nationwide have rallied together to raise funds to help the Muscular Dystrophy…

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Imagining a life without Muscular Dystrophy – Daily Life

Muscular Dystrophy isn’t as well recognised as other afflictions (such as Multiple Sclerosis or Cerebral Palsy), so I often get a blank stare…

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Muscular dystrophy researcher appeals for people to sign up for Town and Gown fundraiser – Oxford Mail

A SCIENTIST who has dedicated her career to finding a cure for muscular dystrophy is backing this year’s Town and Gown fundraising run…

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Merced Lowe’s raises money to send kids with muscular dystrophy to camp – Merced Sun-Star

The Central Valley Chapter of the Muscular Dystrophy Association is teaming up with Lowe’s in Merced to send children with muscle-debilitating diseases to…

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Local leaders to be ‘jailbirds’ for muscular dystrophy – Chambersburg Public Opinion

CHAMBERSBURG – More than 100 local business and community leaders will “do a little time” for those fighting muscular dystrophy and related life-threatening…

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UPDATED: PTC plunges after FDA spurns its failed Duchenne muscular dystrophy drug – FierceBiotech

The FDA is not in a forgiving mood when it comes to biotech companies with bad applications for new drugs for Duchenne muscular…

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FDA Rejects PTC’s New Drug Application for Translarna as a Nonsense Mutation DMD Treatment – Muscular Dystrophy News

Ataluren is a small-molecule protein restoration therapy compound in clinical development for the treatment of Duchenne muscular dystrophy (DMD) caused by a nonsense…

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FDA Asked to Speed Review of New Duchenne MD Treatments in Letter Signed by 109 US Lawmakers – Muscular Dystrophy News

The Muscular Dystrophy Association (MDA) describes Duchenne muscular dystrophy (DMD), one of nine categories of muscular dystrophy, as a genetic disorder characterized by…

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‘Platty’ namesake matched with Ohio preteen with muscular dystrophy – Tulsa World

At the latest camp, Lil Platty picked Brody, a 12-year-old seventh-grader from Columbus, Ohio, with Duchenne Muscular Dystrophy. Although he can walk, Brody…

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Capricor Therapeutics Announces the First Patient with Duchenne Muscular Dystrophy-Related Cardiomyopathy … – PR Newswire (press release)

LOS ANGELES, Feb. 22, 2016 /PRNewswire/ — Capricor Therapeutics, Inc. (NASDAQ: CAPR), a biotechnology company focused on the discovery, development and commercialization of…

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Torrington mother fights for drug to treat her sons with Duchenne muscular dystrophy – FOX 61

TORRINGTON – Both of Melanie Kelly’s sons are in wheelchairs, robbed of their ability to walk, sit-up and bathe themselves. They suffer from…

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Duchenne Muscular Dystrophy – Pipeline Review, H2 2015 – Medgadget.com (blog)

This report provides comprehensive information on the therapeutic development for Duchenne Muscular Dystrophy, complete with comparative analysis at various stages, therapeutics assessment by…

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Firefighters from across the Capital Region camp-out for Muscular Dystrophy – Globalnews.ca

EDMONTON – Firefighters from Edmonton, Strathcona County, Spruce Grove and St. Albert began their annual rooftop campout Sunday morning in support of Muscular…

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Boy appeals to First Minister over muscular dystrophy treatment – Glasgow Evening Times

Problems with heart and lung muscles mean that few born with Duchenne muscular dystrophy currently live to 30. In a letter to the…

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Becker Muscular Dystrophy Global Clinical Trials Review, H2, 2015 – Medgadget.com (blog)

The report, Becker Muscular Dystrophy Global Clinical Trials Review, H2, 2015″ provides an overview of Becker Muscular Dystrophy clinical trials scenario. This report…

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Tarix Orphan Granted Orphan Drug Status for TXA127 as Potential Treatment for Congenital Muscular Dystrophy … – PR Newswire (press release)

17, 2016 /PRNewswire/ — Tarix Orphan LLC today announced that the U.S. Food and Drug Administration has granted Orphan Drug status to the…

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LAMA2 Muscular Dystrophy Drug Candidate TXA127 Is Granted Orphan Drug Status – Muscular Dystrophy News

Tarix Orphan LLC recently announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug designation to TXA127, the company’s lead…

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Muscle Proteins May Serve as Serum Biomarkers for 3 Types of Muscular Dystrophy – Muscular Dystrophy News

Pfizer, in collaboration with Newcastle University, reports finding four serum biomarkers for three types of muscular dystrophy. The markers may be valuable for…

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CSU alum named National Goodwill Ambassador by Muscular Dystrophy Association – Rocky Mountain Collegian

The Muscular Dystrophy Association recently named 2013 Colorado State University alum Joseph Akmakjian its National Goodwill Ambassador. This is the first year the…

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New approach could be used to treat Duchenne muscular dystrophy – News-Medical.net

Scientists at the UCLA Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research and Center for Duchenne Muscular Dystrophy at…

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Muscular dystrophy sufferer James Pendleton, eight, gave amazing answer when told of his condition – Gloucestershire Echo

Treatments for the Muscular Dystrophy are improving all the time and new research is getting closer and closer to finding ever-improving treatments. But…

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Jimboy’s Tacos Raises $11000 for Muscular Dystrophy – QSR magazine (press release) (registration)

Jimboy’s Tacos, the fast-casual, American-style Mexican food chain announced it raised more than $11,000 for the Muscular Dystrophy Association (MDA) during its annual…

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Becker Muscular Dystrophy – Pipeline Review, H2 2015 by ReportBazzar – Medgadget.com (blog)

(RoA) and molecule type, along with latest updates, and featured news and press releases. It also reviews key players involved in the therapeutic…

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Muscular Dystrophy Drugs Face New FDA Questions – Wall Street Journal

Hopes are dimming that the drug industry will be able to quickly deliver a treatment for one of the most keenly researched diseases…

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Pupils ‘Go Orange’ to raise money for muscular dystrophy charity – Gravesend Reporter

Pupils at Shears Green Junior School in Gravesend donned orange clothes on Friday as part of a fundraiser for a muscular disorder charity….

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Stem cell gene therapy could be key to treating Duchenne muscular dystrophy – UC Los Angeles

Scientists at the UCLA Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research and Center for Duchenne Muscular Dystrophy at…

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Man with muscular dystrophy to walk three miles for friend – St Helens Star

AFTER a friend raised money for him last year, a man with muscular dystrophy is taking on a three-mile walk to return the…

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Muscular Dystrophy – Pipeline Review, Industry Analysis, Market Size and Forecast 2016 – 2020 – Medgadget.com (blog)

MRS148 “Muscular Dystrophy Global 2015 Clinical Trials Review, H2” provides an detailed overview of Muscular Dystrophy scenario. Report includes top line data relating…

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Boy With Muscular Dystrophy Writes Heartfelt Note to Scottish Leader – The Mighty

Michael Young, 9, wrote a letter to Scottish first minister Nicola Sturgeon, urging her to help make the drug Translarna available for people…

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Duchenne muscular dystrophy: direct effect on muscle stem cells? An interview with Dr Rudnicki – News-Medical.net

News-Medical.net This understanding is still correct and this is the driver of the muscle damage in Duchenne muscular dystrophy. Our discovery is really a…

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CSU alum named new spokesperson for Muscular Dystrophy Association – Colorado State University News (press release)

Colorado State University News (press release) A Colorado State University alumnus has been named the first adult National Goodwill Ambassador for the Muscular Dystrophy…

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