A researcher at Binghamton University’s Pharmacy School is working on a new drug that could significantly prolong the lives of people with a form of muscular dystrophy.
The school has a pair of researchers working on a breakthrough in the treatment of Duchenne Muscular Dystrophy, a form that affects primarily boys at a rate of about 1 in 5,000.
It’s caused by a lack of a protein that protects muscle tissue.
In 1986, Eric Hoffman, who is now Assistant Dean for Research at BU’s Pharmacy School, discovered the missing gene responsible for Duchenne.
That lead to a drug treatment that allows the body to produce the proteins.
However, the body’s immune system will attack these new proteins, seeing them as foreign.